Mucopolysaccharidosis II

Idursulfase Extends Survival by a Decade in Mucopolysaccharidosis II: Final Results from the 18-Year Hunter Outcome Survey

The final report of the Hunter Outcome Survey (HOS) confirms that idursulfase treatment for Mucopolysaccharidosis II provides a 10-year survival benefit and a 57.9% reduction in mortality risk compared to untreated cohorts, alongside sustai

Breakthrough in Hunter Syndrome: Brain-Penetrant Enzyme Therapy Stabilizes Cognitive Function and Clears Lysosomal Substrates