
Neurologyataxia-telangiectasiaclinical trial
Levacetylleucine Shows Promising Safety and Efficacy in Treating Ataxia-Telangiectasia: Phase 3 Trial Findings
By MedXY|Jul 8, 2026
A phase 3 randomized, placebo-controlled crossover trial demonstrates that levacetylleucine significantly improves neurological function in ataxia-telangiectasia patients with a favorable safety profile.