Diabetes & Endocrinologygenetic short staturegrowth velocity
Vosoritide Shows Promising Growth Benefits in Children with RASopathies and Related Genetic Short Stature Disorders
By MedXY|Aug 18, 2026
A phase II basket trial demonstrates that vosoritide significantly increases growth velocity in children with RASopathies, ACAN, and NPR2 deficiencies, with an acceptable short-term safety profile, suggesting its potential as a precision th